There is currently no cure for cystic fibrosis, but many medications and therapies are available to help patients maintain their health and live longer, more fulfilling lives. Treatment plans are uniquely tailored to each patient’s specific health characteristics and needs.
CFTR Modulators for Cystic Fibrosis
Patients with cystic fibrosis have mutations in the gene that provokes a malfunction of the CFTR protein. Patients usually suffer from a buildup of thick mucus, persistent lung infections, pancreatic damage, and complications in other parts of the body.
In March, the U.K. National Institute for Health and Care Excellence (NICE) issued a draft guidance against recommending Orkambi (lumacaftor-ivacaftor) for treating cystic fibrosis (CF) since its cost is too high for the low benefits it brings.