interview

January 16, 2019January 23, 2019

CFF’s Preston Campbell: 2019 is a ‘Pivotal Year’ for CF Therapies

cystic fibrosis, News

A baby born with cystic fibrosis (CF) today can now expect to live a median 44 years, says Preston W. Campbell, MD, president and CEO of the Cystic Fibrosis ... Read more

October 9, 2018October 9, 2018

Advocacy Groups, Doctors Question Rising Prices of Rare Disease Treatments

cystic fibrosis

Half a year has gone by since disgraced pharma executive Martin Shkreli was sentenced to seven years in federal prison for securities and wire fraud while heading San Diego-based ... Read more

September 10, 2018September 10, 2018

Vertex and Treating CF: 3 Disease-modifying Therapies Make Leap from Lab to Patients

cystic fibrosis, News

Editor’s Note: This is the second of a four-part series looking at Vertex Pharmaceuticals and its “all in for CF” approach. Here, we detail the steps that made three disease-modifying oral ... Read more

August 20, 2018August 20, 2018

Israeli CF Patient Advocacy Group Urges Better Access to Screening, Key Therapies

cystic fibrosis, News

When Shira Zagury joined the Cystic Fibrosis Foundation of Israel as CEO eight years ago, only one cystic fibrosis (CF) patient sat on the nine-member board of directors. Today, five of ... Read more

June 20, 2018June 20, 2018

#ECFS2018 – Phase 2 Trial Supporting SPX-101 as Treatment for All with CF, Spyryx CMO Says

cystic fibrosis, News

SPX-101, designed to help clear mucus from the lungs of people with cystic fibrosis, has the potential to treat all CF patients — regardless of disease-causing mutations. The experimental peptide, which ... Read more

January 30, 2018January 30, 2018

CF Foundation Supports New Clinical Trial of Lenabasum with $25M Award to Corbus

cystic fibrosis, News

Corbus Pharmaceuticals will receive up to $25 million from the Cystic Fibrosis Foundation to help finance a six-month Phase 2b clinical trial of lenabasum (formerly known as anabasum) to ... Read more

November 16, 2017November 16, 2017

Cystic Fibrosis Foundation Helps Patients Through Insurance Maze, and Even with Hurricanes

cystic fibrosis, News

More adults than children are living with cystic fibrosis for the first time ever, says the Cystic Fibrosis Foundation (CFF). This means more patients are encountering issues they have never had ... Read more

November 2, 2017November 2, 2017

Children’s National, NORD Partner to Create Rare Disease ‘Centers of Excellence’

cystic fibrosis, News

Children’s National Health System no longer treats just kids. Its Rare Disease Institute, launched in April 2017, has partnered with the National Organization for Rare Disorders (NORD) to become the ... Read more

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