-
Cystic Fibrosis News Moderator started the topic Renovion's ARINA-1 Shows Promise in CF Mucus Clearance, Study Finds in the forum CF Science and Research 2 years, 8 months ago
A study in cells of CF patients with F508del mutation found ARINA-1 may be better than current options for clearing mucus, especially in combo with Orkambi. Learn more here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Orkambi Benefits CF Patients Across Levels of Lung Health, Study Finds in the forum CF Science and Research 2 years, 8 months ago
A real-world study of Orkambi’s use by 827 patients, including those kept from trials, supported its broad label based on lung function and weight gains. Click here to learn more.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Rage Biotech Opens With Goal of Treating CF and Similar Lung Diseases in the forum CF Science and Research 2 years, 8 months ago
Rage Biotech, building on research done at Australian universities, will focus on a protein that amplifies inflammation to treat inflammatory lung diseases. Read more about this research here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic CF Study Finds P Aeruginosa Mutations May Lead to Biofilm Growth in the forum CF Science and Research 2 years, 8 months ago
Mutations that cause P. aeruginosa to lose motility are linked to higher production of complex sugar molecules involved in biofilm formation, a study says. Find out more here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic COVID-19 Source of Anxiety for Women With CF Children, Survey Finds in the forum CF Science and Research 2 years, 8 months ago
Women caring for their children with cystic fibrosis express greater anxiety related to COVID-19 than the young patients themselves, a survey found. Read the full story here.
Do these findings surprise you? Why or why not?
-
Cystic Fibrosis News Moderator started the topic NHS, Vertex Strike Deal to Make Kaftrio Available in England in the forum CF Science and Research 2 years, 8 months ago
Kaftrio (ivacaftor/tezacaftor/elexacaftor) will be available in England as soon as the medication is approved by the European Commission. Click here to learn more.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic NuvoAir Home Monitoring System Bolsters Telemed Use in CF, Survey Finds in the forum CF Science and Research 2 years, 8 months ago
A survey found cystic fibrosis patients using NuvoAir’s home monitoring system made better use of telemedicine and needed fewer in-person doctor visits. Click here to read more.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Alexion Charitable Foundation Giving $1.1M to Assist Rare Disease Community During Pandemic in the forum CF Science and Research 2 years, 8 months ago
Alexion Charitable Foundation has awarded $1.1 million to NORD and Global Genes to support rare disease patients amid the COVID-19 pandemic. Read the full story here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic CF Trial Resumes Enrollment in Europe, Israel, to Test Eloxx's ELX-02 in the forum CF Science and Research 2 years, 8 months ago
Enrollment has resumed in Eloxx’s trial of ELX-02 for CF in Israel and Europe — but not in the U.S. — after being suspended amid the COVID-19 crisis. Click here to learn more.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic 4DMT Receives Up to $14M from CFF for Development of Customized Gene Carrier in the forum CF Science and Research 2 years, 9 months ago
4D Molecular Therapeutics will receive up to $14 million from the CFF to support the development of a customized gene carrier. Click here to learn more.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Poll Results Highlight Lack of Awareness Cystic Fibrosis in the UK in the forum CF Science and Research 2 years, 9 months ago
Most people in the U.K. are unaware of the challenges faced by people with CF, according to results of a poll commissioned by the Cystic Fibrosis Trust. Read the full story here.
Does this surprise you? Why or why not?
-
Cystic Fibrosis News Moderator started the topic Study: Second-hand Smoke Affects Metabolism in Infants, Children with CF in the forum CF Science and Research 2 years, 9 months ago
Exposure to second-hand smoke is linked to changes in levels of metabolites and activation of signaling pathways that enhance inflammation. Read more here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Coalition Will Address Racial Disparities in Rare Disease Communities in the forum CF Science and Research 2 years, 9 months ago
The Black Women’s Health Imperative has created a Rare Disease Diversity Coalition focused on reducing racial disparities in the rare disease community. Read more about it here.
What are some specific issues you would like the coalition to address?
-
Cystic Fibrosis News Moderator started the topic Kalydeco Approved in Europe to Treat Children With R117H Mutation in the forum CF Science and Research 2 years, 9 months ago
The European Commission has approved Kalydeco (ivacaftor) to treat children and adolescents with CF who carry the R117H mutation in the CFTR gene. Read more here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Home Spirometry Kits for CF Patients Used to Cut Down on Hospital Visits in England in the forum CF Science and Research 2 years, 9 months ago
Thousands of people with cystic fibrosis in England over the age of six will soon be equipped with digital home spirometry kits. Read more here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Quality of Life of CF Children Improved With Mobile PERT App, Study Says in the forum CF Science and Research 2 years, 9 months ago
A study shows that the mobile app MyCyFAPP, which helps patients manage PERT regimens, can improve the quality of life of children with CF with severe GI symptom. Click here to read the full story.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Let's Unite to Ditch the Charade of 'I'm Fine' in the forum Adults With Cystic Fibrosis 2 years, 9 months ago
Lara Govendo believes that vulnerability and unity are key to overcoming struggles. Click here to read more from Lara.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic Georgia College Student Receives AffloVest from Legacy Project in the forum CF Science and Research 2 years, 9 months ago
International Biophysics and the Colton Underwood Legacy Foundation are partnering to deliver the AffloVest to Benjamin Clackum as part of the Legacy Project. Learn more about the project here.
What do you think of this news?
-
Cystic Fibrosis News Moderator started the topic For CF Patients With Pancreatic Insufficiency, Encala Improves Fat Absorption in the forum CF Science and Research 2 years, 9 months ago
Investigational treatment Encala is safe, well tolerated, and increased fat absorption in patients with CF with pancreatic insufficiency, a trial analysis shows. Click here to read more.
What are your thoughts on this study and its findings?
-
Cystic Fibrosis News Moderator started the topic Young CF Patients in UK Receive At-home Lung Monitors Amid COVID-19 in the forum CF Science and Research 2 years, 9 months ago
Oxford Hospitals Charity has purchased and delivered machines able to measure lung function at home to 20 young people with in the U.K. Read the full story here.
What do you think of this news?
- Load More