Seamus Conlan

Kalydeco just got EU commission approval for the Cystic Fibrosis R117h gene alteration – children (please see below):

Kalydeco Approved in Europe to Treat Children with R117H Mutation

This is incredible news for my family and in particular my son Zack.

It is hard to find t…[Read more]

Kalydeco just got EU commission approval for the Cystic Fibrosis R117h gene alteration – children (please see below):

Kalydeco Approved in Europe to Treat Children with R117H Mutation

This is incredible news for my family and in particular my son Zack.

It is hard to find t…[Read more]

The efforts of the Cystic Fibrosis Foundation are encouraging and the new focus on Path to a cure is trying to address one of EmilyKG’s concerns of doing things faster. The Foundation is challenging potential collaborators to submit proposals that will accelerate the pace of progress in CF drug discovery and development and intends to allocate…[Read more]

I believe that funding is key here and all of the CF community must maintain focus on the 10% and follow the lead of the CF Foundation Lab which devotes more than half of its efforts to research focused on nonsense and other rare mutations. I believe the CF community more than any other group fully understand the complexities of CF and have most…[Read more]