Diogo Pinto,  —

Vertex Pharmaceuticals has entered a partnership with the Danish pharmaceutical organization Amgros to one day make Vertex’s cystic fibrosis (CF) therapies available for Danish patients. The collaboration was made through an access contract, a first-of-its-kind contract that gives Danish CF patients access to all Vertex’s current and future CF…

Decibel Therapeutics received worldwide, exclusive rights to develop and commercialize ORC-13661, Oricula Therapeutics’ investigational treatment to prevent hearing loss and balance disorders in patients taking high doses of aminoglycoside antibiotics, including cystic fibrosis (CF) patients. Under the terms of the agreement, Oricula will provide scientific…

A research team at The University of Queensland was honored for its work on the spread of bacteria among cystic fibrosis patients, being named a winner of this year’s Australian Museum Eureka Prizes. The prizes recognize excellence in four fields:  research and innovation, science engagement, science leadership, and science education. CF Air, as…

Pharmaceutical companies Boehringer Ingelheim and Oxford BioMedica are teaming up with the U.K. Cystic Fibrosis Gene Therapy Consortium (GTC) and Imperial Innovations in a collaborative effort to develop a first-in-class, long-term gene therapy to treat cystic fibrosis (CF). The GTC is made up of researchers at Imperial College London and…

Vertex Pharmaceuticals’ Orkambi (lumacaftor/ivacaftor), a licensed medicine used to treat cystic fibrosis (CF) patients ages 6 and older, has now been approved by the U.S. Food and Drug Administration as the first medicine to treat CF in children ages 2-5. The approval is for children who have…

Mologic, an U.K.-based company developing personalized diagnostic devices, announced the beginning of a Phase 1/2 clinical trial to test its urine-based diagnostic tool, HeadsUp, to monitor pulmonary exacerbations in patients with cystic fibrosis (CF). The study is designed to identify biomarkers, present in urine of CF adult patients, that…

Vertex Pharmaceuticals plans to conclude the enrollment of patients in its Phase 3 programs involving its triple combo therapies to treat cystic fibrosis (CF) in the second half of 2018, the company recently announced in a corporate update. This is earlier than expected for the four Phase 3 trials, which…

Grace Rose, a 15-year-old designer who was born with cystic fibrosis (CF), will host the 15th Annual Grace Rose for Cystic Fibrosis Fashion Show Fundraiser on Aug. 18 in Los Angeles to raise funds and awareness about the disease, according to a press release. Taking place at the…

Cystic fibrosis (CF) patients showed improved clinical outcomes and less disease progression after long-term treatment with Kalydeco (ivacaftor), according to an observational study. Researchers found that Kalydeco-treated CF patients had a significantly lower risk of death, pulmonary exacerbation, hospitalization, transplant, and prevalence of CF-related complications and pathological microorganisms,…

Eloxx Pharmaceuticals announced plans to begin Phase 2 studies of ELX-02, its lead candidate to treat cystic fibrosis (CF) and cystinosis, having finished one round of Phase 1 safety and tolerability studies in healthy volunteers. This single, ascending dose study was conducted in a total of 60 people in Israel (NCT02807961)…