News

November 20, 2018November 20, 2018

New Tissue-specific Delivery of CRISPR/Cas9 Aided by Moth Virus and Magnets, Study Shows

cystic fibrosis, News

Rice University researchers are using a virus that infects moths and magnetic nanoparticles to develop a new vehicle for the delivery of CRISPR/Cas9, a genome-editing tool, with high efficiency and ... Read more

November 19, 2018November 19, 2018

Orkambi Closer to Being Approved in Europe to Treat Children Ages 2-5 With Cystic Fibrosis

cystic fibrosis, News

The European Committee for Medicinal Products for Human Use (CHMP) has recommended the approval of Orkambi (lumacaftor/ivacaftor) as a treatment for children ages 2-5 with cystic fibrosis (CF) due to F508del mutations, ... Read more

November 16, 2018November 16, 2018

New Test of Mucus Properties May Help with Coughing and Airway Clearance in CF

cystic fibrosis, News

A new test was able to assess various properties of the mucus that accumulates in the lungs of people with cystic fibrosis and other pulmonary diseases, and may help ... Read more

November 15, 2018November 15, 2018

Ultrasound Predicts Advanced Liver Disease in CF Patients, According to Clinical Trial Data

cystic fibrosis, News

Ultrasound may predict liver disease in young cystic fibrosis (CF) patients, according to the results of a clinical trial. Researchers compared liver patterns from young CF patients, and found ... Read more

November 14, 2018November 14, 2018

Avycaz May Be Effective for Multidrug-resistant P. aeruginosa Infections in CF Patients, Study Suggests

cystic fibrosis, News

Antibacterial Avycaz (ceftazidime-avibactam) showed significant in vitro efficacy against multidrug-resistant Pseudomonas aeruginosa collected from the sputum of cystic fibrosis (CF) patients, according to a recent study. The study, “Multidrug-resistant Pseudomonas aeruginosa from ... Read more

November 12, 2018November 12, 2018

Liver Disease Doesn’t Worsen Lung Function Decline in CF Patients, Study Reports

cystic fibrosis, News

Cystic fibrosis (CF) patients with liver disease do not experience greater lung function decline compared with CF patients without liver presentation, a study reports. The study, “Analysis of a large ... Read more

November 9, 2018November 9, 2018

Majority of CF Patients in Small Study Treated with Antibiotics at Levels Too Low to Fight Lung Infections

cystic fibrosis, News

Ten of 19 cystic fibrosis (CF) patients given antibiotics to manage pulmonary exacerbations did not achieve high enough blood concentrations of the antibiotic to sustain a therapeutic effect, results ... Read more

November 8, 2018November 8, 2018

Worse CF Lung Outcomes Linked with Mutations Causing Iron Overload Disorder, Study Finds

cystic fibrosis, News

Patients with cystic fibrosis (CF) who carry certain mutations in the HFE gene, which are also behind an iron overload disorder, have poorer lung function that declines faster and ... Read more

November 7, 2018November 7, 2018

Anton Yelchin Foundation Donates $1M to USC’s Adult Cystic Fibrosis Clinic at Keck Hospital

cystic fibrosis, News

The Anton Yelchin Foundation has donated $1 million to the University of Southern California (USC) Center for Cystic Fibrosis – Adult Care at Keck Hospital to thank the center for its efforts ... Read more

November 6, 2018November 6, 2018

#NACFC2018 – RPL554 Shows Promising Results in CF Studies

cystic fibrosis, News

Positive data from preclinical and Phase 2a studies evaluating the investigational cystic fibrosis (CF) treatment RPL554 were presented at the 2018 North American Cystic Fibrosis Conference (NACFC) in Denver, Colorado (Oct. ... Read more

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