News

May 23, 2018May 23, 2018

#ATS2018 — Arrowhead’s Investigational CF Treatment ARO-ENaC Shows Potential in Preclinical Studies

cystic fibrosis, News

Arrowhead Pharmaceuticals’ investigational cystic fibrosis treatment candidate ARO-ENaC can effectively target the epithelial sodium channel alpha subunit (αENaC) in the lungs of rats, preclinical studies show. Given that ENaC ... Read more

May 22, 2018May 22, 2018

#ECFS2018 — Celtaxsys Completes Phase 2b Trial Assessing Acebilustat in Cystic Fibrosis Patients

cystic fibrosis, News

Celtaxsys has completed its Phase 2b trial assessing the safety and effectiveness of acebilustat (formerly CTX-4430) for cystic fibrosis (CF), with the company announcing the last visit of the last ... Read more

May 21, 2018May 21, 2018

Triclosan, Antibacterial in Toothpaste, Works Well as Combo Antibiotic Treatment, Study Suggests

cystic fibrosis, News

An antibacterial compound found in toothpaste, called triclosan, may be part of a future cystic fibrosis (CF) treatment, a Michigan State University study suggests. The research, “Triclosan is an ... Read more

May 18, 2018May 19, 2018

#ECFS2018 – Disparities in CF Care Across Europe Focus of ECFS Meeting in Belgrade

cystic fibrosis, News

A baby born with cystic fibrosis (CF) in Germany today is likely to live to be 40 or 50, while another born in the Ukraine will probably die before ... Read more

May 17, 2018May 17, 2018

‘Rare Impact Awards’ Dinner Marks Orphan Drug Act and NORD at 35

cystic fibrosis, News

The National Organization for Rare Disorders (NORD) will celebrate the 35th anniversary of both the 1983 Orphan Drug Act and NORD’s founding at a dinner tonight in Washington, D.C. ... Read more

May 17, 2018May 17, 2018

Long-term Kalydeco Treatment Improves Clinical Outcomes in Cystic Fibrosis Patients, Study Shows

cystic fibrosis, News

Cystic fibrosis (CF) patients showed improved clinical outcomes and less disease progression after long-term treatment with Kalydeco (ivacaftor), according to an observational study. Researchers found that Kalydeco-treated CF patients ... Read more

May 16, 2018May 16, 2018

Once-daily Tobramycin Safe to Treat Flares in Children Under Age 6, Study Says

cystic fibrosis, News

Tobramycin, an antibiotic often used to treat acute lung infections in cystic fibrosis patients, is safe for once-a-day use in children under age 6, with findings of minimal kidney and ... Read more

May 15, 2018May 15, 2018

Gastrointestinal Cancers More Common in Adults with CF, Especially After Transplant, Study Finds

cystic fibrosis, News

Patients with cystic fibrosis (CF) are at higher-than-average risk of developing gastrointestinal cancers, especially those who underwent a lung transplant, a new study shows. Transplant patients with CF were ... Read more

May 14, 2018May 14, 2018

Rally Cycling Team Using Custom Bikes Inspired by Children to Benefit UHCCF

cystic fibrosis, News

A team of professional cyclists are riding six custom-designed and hand-painted bicycles — each inspired by a child whose medical needs were supported by the UnitedHealthcare Children’s Foundation (UHCCF) ... Read more

May 11, 2018May 11, 2018

Proteostasis Appoints 7 CF Experts to Guide Design of PTI-428 Phase 3 Program

cystic fibrosis, News

An advisory committee composed by experts in the field of cystic fibrosis will help to guide the design of the global Phase 3 program testing PTI-428, the company developing the ... Read more

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