When it comes to lung transplants, the Cystic Fibrosis Foundation (CFF) admits that for a long time the…
Articles by Larry Luxner
The Western Hemisphere’s largest gathering of experts in cystic fibrosis gets underway later this month in Nashville, Tennessee —…
Next month’s annual conference of the National Organization for Rare Disorders (NORD) in Washington, D.C., couldn’t come at a…
Developing gene therapies for rare diseases is one thing. Creating gene-edited “designer babies” is quite another. German legal expert Timo…
Imagine living your whole life with a painful disease so rare that only 25 others worldwide have what you have.
Oklahoma suffers more tornadoes than any other state, has the highest per-capita rate of women in U.S. prisons, ranks second…
A new international consortium based in Paris, and funded largely by the 28-member European Union, intends to speed the diagnosis…
A violinist with vasculitis, two Texas politicians and a pharmaceutical company whose marijuana-derived therapy helps kids with Dravet…
RaDaR, the catchy new name for the U.S. government-run Rare Diseases Registry Program, aims to help patient advocacy groups…
With 250 rare diseases newly identified every year, scientists can barely keep up — even as the healthcare system fails…