Patrícia Silva, PhD, director of science content —

Massachusetts-based Vertex Pharmaceuticals, Inc. announced yesterday that they have filed for a New Drug Application (NDA) with the US Food and Drug Administration, and a Marketing Authorization Application (MAA) with the European Medicines Agency (EMA) for their pipeline combination lumacaftor–ivacaftor drug, indicated for the…

Developmental stage biopharmaceutical company Parion Sciences recently announced that the National Institutes of Health‘s grants over the next 5 years in support of pulmonary research programs using their novel pipeline treatments will reach a total of about $15.6 million. These grants have gone to the University of North Carolina,…

Australian specialist pharmaceutical company Pharmaxis has just announced it has successfully enrolled the first participant in an international Phase 3 clinical trial designed to evaluate their lead pipeline product for cystic fibrosis, Bronchitol® (mannitol). Pharmaxis continues to develop novel treatments for chronic respiratory disorders, such as asthma, pulmonary…

Drug discovery company Proteostasis Therapeutics has completed the recruiting process for its Inaugural Cystic Fibrosis Clinical Advisory Board, a new board appointed by the company to act as a strategic resource responsible for the selection of upcoming studies of its compounds for treating cystic fibrosis. The company is dedicated…

McElhattan, Pennsylvania-based Nutek Disposables is conducting a voluntary product recall on the United States for their baby wipes, due to a report of bacteria in some of the packages, which may be dangerous for cystic fibrosis (CF) patients in particular. The wipes were manufactured under the brand names of Cuties,…

Vertex Pharmaceuticals‘ Ivacaftor (Kalydeco), a breakthrough medication for the treatment of patients suffering from a specific gene mutation of cystic fibrosis, has been approved to be added to the list of the Pharmaceutical Benefits Scheme (PBS) in Australia, and will become available on December 1st, as announced by Australian…

Advocates and fundraisers for Cystic Fibrosis continue to develop creative, unique ways to increase awareness of the disease throughout the world and support ongoing clinical research for effective, new therapeutic strategies. Recently, the Cystic Fibrosis Association of New Zealand (CFNZ) joined forces with Ballentynes Fashion Central to organize a fundraising fashion show…

A novel Cystic Fibrosis testing technology that features next-generation DNA sequencing platforms has been launched by Medical Diagnostic Laboratories, L.L.C. Certified by the Clinical Laboratory Improvement Amendments (CLIA) and accredited by the College of American Pathologists (CAP), MDL specializes in complex, state-of-the-art, automated DNA-based molecular analyses. The MDL Cystic Fibrosis Core Test is a CFTR gene sequence exam provided…

Specialty drug discovery company Proteostasis Therapeutics, Inc. has officially welcomed 6 new members to its clinical advisory board, who will have a direct impact on the company’s efforts in developing therapies for cystic fibrosis. The company is internationally known for its focus on developing cutting edge treatments for…

Governor Tom Corbett Every year, millions of babies in the U.S. undergo newborn screening to detect conditions that may gravely affect their health or survival in the long run. This effort is part of healthcare’s emphasis on early detection, accurate diagnoses, and prompt intervention in order to prevent juvenile…