Posts by: Alice Melão

Alice Melão

July 15, 2019July 15, 2019

Babies Treated with Synagis Show No Lasting Benefits in Lung Health as 7-Year-Olds, Real-world Study Finds

cystic fibrosis, News

Treating infants with cystic fibrosis (CF) with the antiviral therapy Synagis (palivizumab) does not improve long-term outcomes in lung health, real-world data show. Routine use of Synagis is not recommended by ... Read more

July 8, 2019July 8, 2019

IMPACT-breath Study Explores Non-invasive Diagnosis of Pseudomonas Aeruginosa Lung Infections in CF Patients

cystic fibrosis, News

The diagnostic potential of breath analysis to detect serious lung infections in people with cystic fibrosis (CF) will be explored in a new clinical trial, which could lead to ... Read more

June 7, 2019June 7, 2019

Inaugural Clairity Ball Celebrating the Life of Claire Wineland Set for June 29

cystic fibrosis, News

Claire’s Place Foundation is throwing an inaugural fundraising ball June 29 to celebrate the life and legacy of the foundation’s late founder, Claire Wineland, who had cystic fibrosis (CF). ... Read more

June 6, 2019June 6, 2019

Investigational CFTR Amplifier PTI-428 Receives Orphan Drug Status in Europe

cystic fibrosis, News

Proteostasis Therapeutics received orphan drug designation from the European Commission for its investigational CFTR amplifier PTI-428 in development for the treatment of cystic fibrosis (CF). This recognition of the therapeutic ... Read more

May 15, 2019May 15, 2019

Early, Rapid BMI Increase May Affect Overall Growth of CF Children, Study Suggests

cystic fibrosis, News

Rapid weight gain early in life may have a long-term negative impact on the growth of children with cystic fibrosis (CF), a study has found. This finding suggests that ... Read more

March 27, 2019May 17, 2019

Triple Combo of Proteostasis’ CFTR Modulators May Benefit CF Patients, Phase 1 Trial Shows

cystic fibrosis, News

Treatment with Proteostasis Therapeutics’ triple combo therapy regimen may significantly improve the lung function of patients with cystic fibrosis (CF), results from a Phase 1 clinical trial suggest. The ... Read more

March 25, 2019May 15, 2019

Targeting Bacteria Cell Wall Elements Can Fight Chronic P. aeruginosa Infection, Study Suggests

cystic fibrosis, News

Targeting some elements in the bacterial cell wall can be an effective way to activate the immune system and fight chronic, treatment-resistant Pseudomonas aeruginosa infections, according to a study. ... Read more

March 8, 2019March 26, 2019

Positive Data from VX-445 Triple Combo Regimen Prompt Vertex to Seek Regulatory Approval

News

Vertex Pharmaceuticals is planning to request regulatory approval from the U.S. Food and Drug Administration (FDA) and the European Medicines Agency (EMA) during the third and fourth quarters of 2019, ... Read more

March 6, 2019March 19, 2019

Translate Bio Advancing MRT5005 Through Ongoing Phase 1/2 Trial in CF Patients

cystic fibrosis, News

An ongoing Phase 1/2 clinical trial exploring Translate Bio’s investigational therapy MRT5005 will start testing multiple ascending doses (MAD) in patients with cystic fibrosis (CF). This follows an assessment ... Read more

March 4, 2019March 19, 2019

European HIT-CF Project to Explore ELX-02 as Treatment for Rare CF Mutations

cystic fibrosis, News

Eloxx Pharmaceuticals will explore the potential of its lead investigational drug candidate, ELX-02, as a treatment for patients with cystic fibrosis (CF) caused by rare nonsense genetic mutations, in new ... Read more

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