Proteostasis Therapeutics, Inc. (PTI), a company that develops disease-modifying therapeutics for diseases involving protein processing, recently announced at a presentation during the 29th Annual North American Cystic Fibrosis Conference data on its transmembrane conductance regulator (CFTR) amplifier program for use in combined treatments for patients with cystic fibrosis (CF). In…
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Alcresta, a company dedicated to developing and commercializing novel enzyme-based products that address the challenges faced by patients with gastrointestinal disorders and rare diseases such as cystic fibrosis recently presented at the 29th Annual North American Cystic Fibrosis Conference (NACFC) new clinical results reporting on its product and technology. The conference is taking…
Celtaxsys, a pharmaceutical company focused on novel therapeutics to treat inflammatory diseases, announced that it is beginning enrollment of patients for a phase 2 clinical trial to test the efficacy of acebilustat in patients with cystic fibrosis (CF). The study will be conducted in the United States and European Union…
Concert Pharmaceuticals will present data from a Phase 1 single ascending dose trial of experimental CF therapy CTP-656, a next generation potentiator developed for the treatment of cystic fibrosis during the 29th Annual North American Cystic Fibrosis Conference this week in Phoenix, Arizona. The study being presented is entitled ”…
This week, Vertex Pharmaceuticals Incorporated, a global biotechnology company that aims to discover, develop and commercialize innovative new medicines for diseases such as cystic fibrosis, announced that the U.S. Food and Drug Administration (FDA) has accepted for review a supplemental New Drug Application (sNDA) for the use of…
Researchers at Claremont, California-based biotechnology company Synedgen are developing targeted therapies that address complications of cystic fibrosis (CF) on pulmonary and GI surfaces for which only limited treatment options are currently available — an unmet need frequently leading to early mortality. CF is a genetic disease caused by mutations in…
Mechelen, Belgium-based biotech company Galapagos NV is presenting promising research findings at this year’s North American Cystic Fibrosis Conference (NACFC), which is currently underway in Phoenix, Arizona. The clinical-stage company, which specializes in the discovery and development of small molecule medicines with novel modes of action to treat diseases like…
Quest Diagnostics recently announced findings from several research projects detailing the clinical value of genetic tests to help predict or detect diseases. Data from the studies, which are being presented at the 2015 American Society of Human Genetics (ASHG) Annual Meeting being held Baltimore, Maryland from October 8-10, 2015, show that screening…
Pulmatrix, Inc. released animal-based research data at the 2015 North American Cystic Fibrosis Conference indicating that PUR1900 (iSPERSE™-formulated itraconazole) helped fight against Aspergillus fumigatus in rats. The fungus causes lung infection in cystic fibrosis. Concentrations of PUR1900 were high in the lungs but low in the overall body of the rats, indicating that…
Boulder, Colorado based Nivalis Therapeutics, Inc. a clinical stage pharmaceutical company focused on treating people with cystic fibrosis (CF), is reporting positive topline results from a Phase 1b clinical study evaluating its Cystic Fibrosis drug candidate N91115 — a novel stabilizer of the cystic fibrosis transmembrane conductance regulator (CFTR)…
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