#TBT – Cystic Fibrosis Patient Testimony on Orkambi

admin avatar

by admin |

Share this article:

Share article via email

https://www.youtube.com/watch?v=3ARdU_FVAgA

Orkambi is a combination therapy for treatment of cystic fibrosis. The FDA approval for the therapy was announced on July 2nd, 2015.

Learn more about Orkambi here.

In this StratAcuity: The Science of People video, watch this Orkambi testimony before the Open Public Hearing OPH portion of the May 12, 2015, Pulmonary-Allergy Drugs Advisory Committee (PADAC) meeting in Washington, D.C. by cystic fibrosis patient Kate Marshall.

The 15-year-old has two copies of the D508 gene, which Orkambi, (the combination of Ivacaftor and Lumacaftor) treats.

In March, the U.K. National Institute for Health and Care Excellence (NICE) issued a draft guidance against recommending Orkambi (lumacaftor-ivacaftor) for treating cystic fibrosis (CF) since its cost is too high for the low benefits it brings.

Cystic Fibrosis News Today is strictly a news and information website about the disease. It does not provide medical advice, diagnosis or treatment. This content is not intended to be a substitute for professional medical advice, diagnosis, or treatment. Always seek the advice of your physician or another qualified health provider with any questions you may have regarding a medical condition. Never disregard professional medical advice or delay in seeking it because of something you have read on this website.


Featured Column

How I Discovered That PTSD Was Causing My Post-transplant Struggles

PTSD, mental health, communities, stress, grateful, work, trauma, rare disease day, transplant, CF community, National Blood Donor Month, birthdays, holidays
Columnist Lara Govendo addresses an issue that several readers may relate to: post-transplant PTSD, which can wreak havoc.

Read the Column


Your CF Community


Visit the Cystic Fibrosis News Today forums to connect with others in the CF community.