A new survey conducted in Germany showed that, in addition to easing symptoms and improving quality of life, Trikafta enables most patients with cystic fibrosis (CF) to reduce the use of supportive therapies, according to a study. However, this is being done without clear guidelines. “We think it best…
Researchers in Australia have identified six potential genes that may help explain why people with cystic fibrosis (CF) experience pain — and respond to pain treatments — differently. The genes — CTRC, SPINK1, TNF, ABCB1, PRSS1, and TGFB1 — were found to interact with CFTR, the gene whose mutations…
The experimental inhaled gene therapy 4D-710 showed acceptable safety and signs of improving lung function in adults with cystic fibrosis (CF), according to new Phase 1 clinical trial data. Developer 4D Molecular Therapeutics (4DMT) has now selected the study’s lowest dose for further evaluation in a Phase 2…
Discussion
People always say kids are resilient. I used to nod politely, not really knowing what they meant. But then I had Jasmine, my daughter with cystic fibrosis, and life rewrote the definition right in front of me. At 4, she already knew her routines better than most adults.
Becoming educated and informed about cystic fibrosis is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your CF journey.
There is no cure for CF yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
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