ProQR Therapeutics says its investigational drug QR-010 improved respiratory symptoms in 70 adults with cystic fibrosis (CF) who participated in a…
Articles by Magdalena Kegel
4D Molecular Therapeutics (4DMT) announced it has secured funding to complete studies necessary for its gene therapy candidate for…
Good nutrition may slow the progression of cystic fibrosis patients’ lung disease, according to a review by researchers at the…
Some children with severe infections who require intravenous antibiotics can be treated safely at home, according to a review of…
Scientists have long known that defects in the CFTR protein cause cystic fibrosis. Now they’ve discovered that the defective protein leads…
Vertex Pharmaceuticals is continuing to develop treatments for all people with cystic fibrosis (CF), with clinical trials exploring combinations of…
Relizorb, an enzyme-containing cartridge that breaks down fats in tube-feeding formulas, is now available to children, according to its developer, Alcresta Therapeutics.
The U.S. Food and Drug Administration (FDA) has approved Digestive Care’s Pertzye (pancrelipase) to be given to cystic fibrosis…
Three triple-combination treatments from Vertex Pharmaceuticals showed promising results in Phase 1 and Phase 2 clinical trials in cystic fibrosis (CF) patients…
The U.S. Food and Drug Administration is promoting a targeted treatment approach known as precision medicine to help people with…