The Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency has adopted a positive opinion…
Articles by Marisa Wexler, MS
Vertex Pharmaceuticals announced a multiyear partnership with Affinia Therapeutics to develop gene therapies for cystic fibrosis (CF) and other…
Orkambi (ivacaftor/lumacaftor) can improve glucose tolerance in people with cystic fibrosis, a small study in patients either at…
Supplemental estrogen, most commonly taken for contraception, is associated with poorer bone mineral density in people with cystic fibrosis…
A measure called the lung clearance index (LCI) can predict low blood oxygen levels during sleep in people with…
Delivering nutrients through dialysis could help people with co-occurring cystic fibrosis (CF) and kidney disease meet their nutritional requirements,…
An unusual clinical presentation can hinder proper diagnosis for people with cystic fibrosis (CF), even with newborn screening, a…
Liver ultrasounds can help identify children with cystic fibrosis (CF) who are at higher risk of developing liver disease,…
The U.S. Food and Drug Administration (FDA) has granted fast track designation to MRT5005, an investigational RNA-based…
Enrollment is complete for a European initiative to test an organoid-based, personalized-medicine approach to treating cystic fibrosis, with the…