News

October 7, 2019October 7, 2019

5,000 Expected to Attend Cystic Fibrosis Conference, NACFC 2019, in Nashville

cystic fibrosis, News

The Western Hemisphere’s largest gathering of experts in cystic fibrosis gets underway later this month in Nashville, Tennessee — site of the 33rd annual North American Cystic Fibrosis Conference ... Read more

October 3, 2019October 3, 2019

Vertex Partners with Ribometrix to Discover RNA-targeted Therapies

cystic fibrosis, News

Vertex Pharmaceuticals has entered a strategic collaboration with Ribometrix to discover potential RNA-targeted therapies for serious diseases. Vertex is a leader in the market of CFTR modulators for cystic fibrosis (CF), and is ... Read more

October 2, 2019October 2, 2019

Hexoskin Smart Shirt Can Accurately Assess Respiratory Function, May Be Tool in CF, Study Shows

cystic fibrosis, News

Using a simple shirt — a smart one — is closer to becoming a common method to measure lung function in patients with respiratory conditions, including chronic obstructive pulmonary ... Read more

October 1, 2019October 1, 2019

IL-1 Receptor Inhibition a Potential Strategy to Block Mucus Build-up in Early CF, Study Suggests

cystic fibrosis, News

Inhibition of the interleukin-1 receptor — to block thick mucus production and inflammation — is a potential strategy to treat cystic fibrosis (CF) in the early stages of the ... Read more

September 30, 2019September 30, 2019

Public Encouraged to Vote for 2 Students with CF to Receive $22K AbbVie Scholarships

cystic fibrosis, News

Voting for two students to receive two scholarships — valued at $22,000 each — is now open to the public until Oct. 9, pharmaceutical company AbbVie has announced. After ... Read more

September 27, 2019September 27, 2019

AzurRx BioPharma Announces Promising Results from Trial Testing MS1819 for EPI in CF Patients

cystic fibrosis, News

The investigational therapy MS1819 showed positive safety results in a Phase 2 clinical trial for the treatment of exocrine pancreatic insufficiency (EPI) in people with cystic fibrosis (CF), AzurRx BioPharma ... Read more

September 26, 2019September 26, 2019

NORD 2019 Rare Disease Summit Set for Oct. 21-22 in Washington, DC

cystic fibrosis, News

Next month’s annual conference of the National Organization for Rare Disorders (NORD) in Washington, D.C., couldn’t come at a better time, says Marshall Summar, MD, chairman of NORD’s board ... Read more

September 26, 2019September 26, 2019

Professor Launches Research Initiative to Encourage Students to Develop and Test Antibiotics for CF Infections

cystic fibrosis, News

Kristen Mudrack, PhD, a chemistry professor at Milligan College in Tennessee, has launched a research initiative to encourage college students to produce and test antibiotics that target and destroy ... Read more

September 25, 2019September 25, 2019

CF Foundation Awards Eloxx $1.61M for Phase 2 Trials in People with Nonsense Mutations

cystic fibrosis, News

The Cystic Fibrosis Foundation (CFF) is giving Eloxx Pharmaceuticals up to $1.61 million to support its planned Phase 2 clinical trial program assessing the safety, tolerability, and chemical properties of ... Read more

September 24, 2019September 24, 2019

Kalydeco’s Efficacy Tied to Phosphorylation Levels of CFTR Protein, Study Suggests

cystic fibrosis, News

CFTR channel activity is controlled by a molecular process known as phosphorylation. Now, a study suggests that the levels of phosphorylation affect how well Kalydeco works in people with certain mutations in ... Read more

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