News

January 29, 2019February 6, 2019

Toddlers Age 1-2 With CF Can Now Be Treated With Kalydeco in Canada

cystic fibrosis, News

Health Canada has approved the use of Kalydeco (ivacaftor) in toddlers age 1-2 years with certain genetic mutations that prevent the correct functioning of the CFTR protein, the therapy’s developer ... Read more

January 28, 2019February 1, 2019

Personalized Nutrition Programs May Help Improve Outcomes for CF Patients, Survey Suggests

cystic fibrosis, News

New personalized strategies that can address the nutritional needs of cystic fibrosis patients may provide the best care and improve patient outcomes, a study suggests. The study, “A survey ... Read more

January 25, 2019February 4, 2019

CF Foundation Gives $4.5M to Expedite Talee Bio’s Development of Two Gene Therapy Candidates

cystic fibrosis, News

The Cystic Fibrosis Foundation (CFF) will fund the preclinical development of two gene therapy candidates, Talee Bio’s TL-101 and TL-102, for the treatment of cystic fibrosis (CF), the company announced. ... Read more

January 24, 2019February 5, 2019

European Research Team Granted €6.8M to Develop Non-viral Gene Therapy System

cystic fibrosis, News

The Horizon 2020 research and innovation program of the European Union granted €6.8 million (approximately $7.7 million) to an international research team for the development of non-viral gene delivery ... Read more

January 23, 2019January 31, 2019

Orkambi Approved in Europe for Younger CF Patients with F508del Mutations

cystic fibrosis, News

The European Commission has approved the label extension of Orkambi (lumacaftor/ivacaftor) for the treatment of children ages 2-5 with cystic fibrosis (CF) due to F508del mutations, Vertex Pharmaceuticals, the ... Read more

January 22, 2019January 31, 2019

CF Patients Navigate Increasingly Complex Health Insurance Quagmire

cystic fibrosis, News

Florida resident Megan Willis has cystic fibrosis (CF), and she’s not getting better. But that didn’t stop authorities last March from deciding otherwise, and denying her access to Medicaid ... Read more

January 22, 2019January 31, 2019

Woman’s Lawsuit Put Emphasis on ‘Urgency’ in Deciding Organ Transplants in US

cystic fibrosis, News

Waiting for a lung transplant in the intensive care unit at a New York hospital in November 2017, a 21-year-old pulmonary hypertension patient named Miriam Holman sued the U.S. ... Read more

January 18, 2019January 29, 2019

Non-invasive Ventilation Improves Lung Function in CF Patients But Not Survival, Study Finds

cystic fibrosis, News

A reassessment of U.K. medical records showed that in cystic fibrosis (CF) patients, breathing support provided by gas inhalation, through a face or nasal mask, helps improve lung function ... Read more

January 17, 2019January 24, 2019

Phase 2 Trial Testing SPI-1005 for Ototoxicity in CF Patients Moving Forward

cystic fibrosis, News

Sound Pharmaceuticals (SPI) has enrolled its first-patient-in — meaning the first subject meeting the criteria for inclusion and exclusion of a clinical study — in a Phase 2 trial ... Read more

January 16, 2019January 23, 2019

CFF’s Preston Campbell: 2019 is a ‘Pivotal Year’ for CF Therapies

cystic fibrosis, News

A baby born with cystic fibrosis (CF) today can now expect to live a median 44 years, says Preston W. Campbell, MD, president and CEO of the Cystic Fibrosis ... Read more

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