cystic fibrosis

June 22, 2020June 22, 2020

Alexion Charitable Foundation Giving $1.1M to Assist Rare Disease Community During Pandemic

The Alexion Charitable Foundation has awarded $1.1 million in grants to programs that support those with rare diseases during the COVID-19 pandemic, the organization recently announced. The grants will ... Read more

June 22, 2020June 22, 2020

Eloxx Resumes Enrollment in Phase 2 Trial of ELX-02 in Europe, Israel

cystic fibrosis, News

Eloxx Pharmaceuticals has resumed enrollment in its Phase 2 clinical trial evaluating ELX-02 in cystic fibrosis (CF) patients in Israel and Europe, after it was temporarily halted due to ... Read more

June 19, 2020June 19, 2020

4DMT Receives Up to $14M from CFF for Development of Customized Gene Carrier

cystic fibrosis, News

After being given more than $3 million from the Cystic Fibrosis Foundation (CFF) in 2017 to expand the development of viral vectors for gene delivery in the lungs, 4D ... Read more

June 18, 2020June 18, 2020

Poll Results Highlight Lack of Awareness About Cystic Fibrosis in the UK

cystic fibrosis, News

Most people in the U.K. are unaware of the challenges faced by people living with cystic fibrosis (CF), according to results of a YouGov poll commissioned by the U.K. Cystic Fibrosis ... Read more

June 17, 2020June 17, 2020

Second-hand Smoke Affects Metabolism in Infants and Children with CF, Study Finds

cystic fibrosis, News

Exposure to second-hand smoke in infants and children with cystic fibrosis (CF) is linked to changes in levels of metabolites and activation of signaling pathways that enhance inflammation, a ... Read more

June 16, 2020June 16, 2020

3rd Annual CF FamilyCon, Free and Online, Starts Thursday

cystic fibrosis, News

The third annual CF FamilyCon, a free and online event that connects people with cystic fibrosis (CF) and their extended families and friends with one another — and to ... Read more

June 15, 2020June 15, 2020

New Combination of CFTR Mutations Found in Chinese Siblings With CF

cystic fibrosis, News

A combination of two mutations, including one that had never been reported, were found in two Chinese siblings who developed a severe form of cystic fibrosis (CF), according to ... Read more

June 12, 2020June 12, 2020

England Using Home Spirometry Kits to Cut Down on Hospital Visits

cystic fibrosis, News

Thousands of people in England with cystic fibrosis (CF) soon will be equipped with digital home spirometry kits. This will allow patients age 6 and older to monitor and ... Read more

June 11, 2020June 11, 2020

Kalydeco Approved in Europe to Treat Children with R117H Mutation

cystic fibrosis, News

The European Commission has approved Vertex’s Kalydeco (ivacaftor) for the treatment of children and adolescents with cystic fibrosis (CF) who carry the R117H mutation in the cystic fibrosis transmembrane ... Read more

June 9, 2020June 15, 2020

Suppressing Function of Chloride Channel TMEM16A Eyed as Potential Therapeutic Approach

cystic fibrosis, News

Researchers have reported the case of two siblings with impaired CFTR function due to a deficiency in another chloride channel, called TMEM16A, that do not present symptoms associated with ... Read more