cystic fibrosis

January 15, 2019January 15, 2019

Immunotherapy May Be Promising Strategy to Treat Chronic Infections of P. aeruginosa in CF Patients

cystic fibrosis, News

Blocking the interaction between two molecules involved in immune restraining mechanisms — called PD-1 and PD-L1 — may be an effective therapeutic strategy to boost the immune system and ... Read more

January 14, 2019January 14, 2019

Eluforsen Improves CFTR Protein Function in CF Patients with F508del Mutations, Phase 1 Trial Shows

cystic fibrosis, News

An exploratory Phase 1 trial showed that repeated intranasal treatment with the therapy eluforsen improved CFTR protein activity in adults with cystic fibrosis (CF) carrying F508del mutations in both ... Read more

January 11, 2019January 11, 2019

WHO Approves Ensifentrine as Name for Potential Inhaled Treatment Now in Clinical Trials

cystic fibrosis, News

The World Health Organization (WHO) approved ensifentrine as the recommended name to identify the cystic fibrosis (CF) treatment candidate RPL554. Verona Pharma’s ensifentrine is an inhaled inhibitor of the enzymes phosphodiesterase ... Read more

January 10, 2019January 10, 2019

New Inhaled Carrier May Work for CF mRNA Therapy, Mouse Study Finds

cystic fibrosis, News

An inhaled form of messenger RNA (mRNA) with the potential to safely deliver therapeutics to the lungs of cystic fibrosis (CF) patients has been discovered by researchers at the ... Read more

January 9, 2019January 9, 2019

Alcresta’s Relizorb Given Medicare/Medicaid Billing Code for Easier Claims

cystic fibrosis

The Centers for Medicare and Medicaid Services (CMS) has issued a permanent billing code (B4105) to Alcresta Therapeutics’ in-line digestive enzyme cartridge Relizorb, making it easier for insurance payers ... Read more

January 8, 2019January 14, 2019

Vertex and Arbor Biotechnologies Collaborating to Develop Cystic Fibrosis Gene Therapies

cystic fibrosis, News

Vertex Pharmaceuticals and Arbor Biotechnologies have established a partnership to discover new proteins to advance the development of gene therapies for cystic fibrosis. The companies also plan to develop ... Read more

January 4, 2019January 15, 2019

Claire’s Place Foundation Grants to Help CF Families Reaches $1 Million Milestone

cystic fibrosis

After eight years of easing the financial burden of protracted hospital stays, Claire’s Place Foundation has reached the $1 million mark in assistance to families living with cystic fibrosis (CF). The ... Read more

January 3, 2019January 11, 2019

Vertex to Request Review of Orkambi, Symkevi Plus Kalydeco for Public Funding in Scotland

cystic fibrosis

Vertex Pharmaceuticals has announced its intention to submit an application to the Scottish Medicines Consortium (SMC) to review the clinical and cost-effectiveness of the company’s cystic fibrosis (CF) medicines, Orkambi (lumacaftor/ivacaftor), as well ... Read more

January 2, 2019January 8, 2019

AzurRx Starts Phase 2 Clinical Trial Testing MS1819-SD in CF Patients With EPI

cystic fibrosis, News

AzurRx BioPharma announced it has started a Phase 2 clinical trial testing the safety, tolerability, and efficacy of MS1819 Spray Dried (MS1819-SD) therapy in cystic fibrosis (CF) patients with ... Read more

cystic fibrosis

Immunotherapy May Be Promising Strategy to Treat Chronic Infections of P. aeruginosa in CF Patients

Eluforsen Improves CFTR Protein Function in CF Patients with F508del Mutations, Phase 1 Trial Shows

WHO Approves Ensifentrine as Name for Potential Inhaled Treatment Now in Clinical Trials

New Inhaled Carrier May Work for CF mRNA Therapy, Mouse Study Finds

Alcresta’s Relizorb Given Medicare/Medicaid Billing Code for Easier Claims

Vertex and Arbor Biotechnologies Collaborating to Develop Cystic Fibrosis Gene Therapies

Claire’s Place Foundation Grants to Help CF Families Reaches $1 Million Milestone

Vertex to Request Review of Orkambi, Symkevi Plus Kalydeco for Public Funding in Scotland

Top 10 Cystic Fibrosis Stories of 2018

AzurRx Starts Phase 2 Clinical Trial Testing MS1819-SD in CF Patients With EPI

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