cystic fibrosis

May 20, 2019May 20, 2019

Vivus Announces Partnership with HarborPath to Make Pancreaze Available to Uninsured Patients

cystic fibrosis, News

Vivus recently announced a partnership with HarborPath Direct to facilitate access to Pancreaze (pancrelipase) for eligible patients who do not have health insurance or are underinsured. The treatment will be ... Read more

May 17, 2019May 17, 2019

Rare Diseases Constitute a ‘Public Health Issue,’ NCATS Director Warns

cystic fibrosis

With 250 rare diseases newly identified every year, scientists can barely keep up — even as the healthcare system fails millions of Americans whose rare diseases have already been ... Read more

May 16, 2019May 16, 2019

Bike Rides, Walkathons, Other Fundraising Events Mark CF Awareness Month

cystic fibrosis, News

When it comes to disease “awareness” days, weeks, and months, 2019 is crammed with hundreds of them. May leads the calendar with 37 such designations, calling attention to everything from ... Read more

May 16, 2019May 16, 2019

Poor Oxygen Conditions May Promote P. aeruginosa Infection Over Other Pathogen in CF, Study Suggests

cystic fibrosis, News

Poor oxygen conditions, a common trait in the lungs of cystic fibrosis (CF) patients, may help Pseudomonas aeruginosa bacteria outcompete other infectious agents, namely Staphylococcus aureus, a study suggests. The ... Read more

May 15, 2019May 15, 2019

Early, Rapid BMI Increase May Affect Overall Growth of CF Children, Study Suggests

cystic fibrosis, News

Rapid weight gain early in life may have a long-term negative impact on the growth of children with cystic fibrosis (CF), a study has found. This finding suggests that ... Read more

May 14, 2019May 14, 2019

Phages, Viruses that Attack Bacteria, Are a Potential Therapy Against Infections, Case Report Suggests

cystic fibrosis, News

The case report of a cystic fibrosis (CF) patient suggests that phages — viruses that naturally infect and kill bacteria — are a potential personalized therapy against infections caused ... Read more

May 13, 2019May 13, 2019

Trial of Nebulized CF Candidate Therapy Completes Single-ascending Dosing

cystic fibrosis, News

The RESTORE-CF clinical trial investigating Translate Bio’s candidate therapy MRT5005 has completed the single-ascending dose regimen in patients with cystic fibrosis (CF), the company announced. The ongoing Phase 1/2 trial (NCT03375047) is testing the safety ... Read more

May 10, 2019May 10, 2019

ABO-401 Gene Therapy Shows Potential to Restore CFTR Function in Preclinical Study

cystic fibrosis, News

Abeona Therapeutics‘ new gene therapy ABO-401 for the treatment of cystic fibrosis (CF) has successfully delivered a functional version of the CFTR gene to the lungs of mice with CF, according to ... Read more

May 8, 2019May 8, 2019

NFL’s Boomer Esiason Will Be Keynote Speaker at NASP Annual Meeting

cystic fibrosis, News

Former National Football League quarterback Boomer Esiason, whose son has cystic fibrosis (CF), will be a keynote speaker at the National Association of Specialty Pharmacy’s (NASP) Annual Meeting & ... Read more

May 7, 2019May 7, 2019

Motif Bio, Lamellar Agree to Test New Therapeutic Combo for CF Lung Infections

cystic fibrosis

Motif Bio has entered an agreement with Lamellar Biomedical to undertake a preclinical study that will test a new therapeutic combination for treating lung infections in patients with cystic fibrosis ... Read more

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